Frequently asked questions

...can I learn more about this study? You can learn more about this study at www.DuchenneConnect.org, www.muscular-dystrophy.org and www.for-dmd.org. It will be listed on www.clinicaltrials.gov nearer the recruitment start date.... Read more »

Protocol – questions and answers

...GCP and paediatric guidelines in research, you are not allowed to collect more than 1-1.5 ml/kg within 24 hours for research studies in paediatric population. The urine sample for bone-DMD... Read more »

Hints and updates

...appear. This discrepancy is because rather than have 10 separate data entry screens for each combination of age group and parent/child we opted to combine them into two (Core and... Read more »